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CMT1A Clinical Trial and Drug Development Update
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Ай бұрынCMT Research Foundation recently hosted a webinar featuring Dr. Jorge A. Quiroz (NMD Pharma), Dr. Carlos Loya (82VS, an Alloy Therapeutics, Inc. Venture Studio) and Peter deSilva (CMTRF Board Chair and ENDGAME Chair). The webinar highlighted two major events that are underway for CMT.
Dr. Quiroz spoke about NMD Pharma receiving approval to initiate a Phase 2 clinical trial of NMD670 in patients living with CMT types 1 and 2.
Dr. Loya spoke about a new technology for CMT drug development and highlighted the delivery vehicle designed to carry genetic therapies to the peripheral nervous system
For more information, visit cmtrf.org/endgame.
@twistnbend4jewlz 12 күн бұрын
I wish these trials were offered in Canada
@MdAlif-j7l 27 күн бұрын
Dear, I am 21 year aged I am hearing form the age of 15 please do something because I can see how my life is ruin after few year I will be unable to walk.
@MdAlif-j7l 27 күн бұрын
How much time it will take I am I am hearing it from the age of 15 and now I am 21 can you please tell me ?
@cmtresearchfoundation 17 күн бұрын
Determining how long a drug development program will take to become an approved drug is challenging because each program is unique and it's unpredictable if a drug will meet the necessary milestones for approval. CMTRF currently has 5 CMT projects that have resulted in drug candidates that are now moving towards clinical trials and we aim to continue to fund more projects to increase the chances of getting approved treatments for CMT. If you would like to stay updated on the progress of these projects, please visit cmtrf.org/ and sign up for our email mailing list.
@ShuvamDadal Ай бұрын
can gene therapy stop the progression of cmt?😂
@cmtresearchfoundation 17 күн бұрын
Genetic medicines have the potential to stop or even reverse the progression of diseases because they target the underlying genetic cause. This makes them promising therapeutic approaches to explore for CMT. As of today, CMTRF has funded 11 projects that explore various genetic technologies for CMT. To date, these projects have resulted in 3 genetic-based drug candidates that are now moving forward towards human clinical trials. For more information on genetic medicines and to stay up to date on all the CMT genetic-based therapy projects we fund, please visit cmtrf.org/gene-therapy/
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